By: Ian Sample Science editor | Gene therapy could treat rare brain disorder in unborn babies | Neuroscience | The Guardian
Doctors could use Crispr tool to inject benign virus into foetus’s brain to ‘switch on’ key genes
Scientists are developing a radical form of gene therapy that could cure a devastating medical disorder by mending mutations in the brains of foetuses in the womb.
The treatment, which has never been attempted before, would involve doctors injecting the feotus’s brain with a harmless virus that infects the neurons and delivers a suite of molecules that correct the genetic faults.
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